Metabolic Disorders
50 medicines listed.
Aldurazyme
Laronidase
By Sanofi (via Genzyme/BioMarin)
Vial · from 1 per pack
Brand $1,115.00
Amvuttra
Vutrisiran
By Alnylam Pharmaceuticals
Pack · from 1 per pack
Brand $166,475.00
Carbaglu
Carglumic Acid
Pack sizes and pricing not listed yet
Cerdelga
Eliglustat
By Genzyme
Capsules · from 56 per pack
Brand $34,500.00
Cerezyme
Imiglucerase
By Genzyme
Pack · from 1 per pack
Brand $2,745.00
Crysvita
Burosumab
By Piramal Healthcare
Vial · from 1 per pack
Brand from $5,225.00
Cystadane
Betaine Anhydrous
By AOP Orphan
Pack · from 1 per pack
Brand $900.00
Cystagon
Cysteamine Bitartrate
By Mylan
Capsules · from 100 per pack
Brand $450.00
Dojolvi
Triheptanoin
By Ultragenyx
Pack · from 1 per pack
Brand $12,350.00
Dostinex
Cabergoline
By Pfizer
Tablets · from 2 per pack
Brand from $32.00
Elaprase
Idursulfase
By Takeda
Pack · from 6 per pack
Brand $4,920.00
Elelyso
Taliglucerase Alfa
By Pfizer
Pack · from 1 per pack
Brand $1,675.00
Fabrazyme
Agalsidase Beta
By Sanofi
Vial · from 35 per pack
Brand $5,390.00
Galafold
Migalastat Hydrochloride
By Amicus Therapeutics
Tablets · from 14 per pack
Brand $34,065.00
GIVLAARI
Givosiran Sodium
By UNKNOWN
Vial · from 1 per pack
Brand $84,035.00
Isturisa
Osilodrostat
By Recordati
Tablets · from 60 per pack
Brand from $2,925.00
Kanuma
Sebelipase Alfa
By Alexion Pharmaceuticals
Vial · from 1 per pack
Brand $14,435.00
Kayexalate Powder
Polystyrene Sulphonate
By Sanofi
Bottle · from 1 per pack
Brand $83.00
KUVAN
Sapropterin Dihydrochloride
By BioMarin
Tablets · from 30 per pack
Brand from $785.00
Lamzede
Velmanase alfa
By Chiesi
Vial · from 1 per pack
Brand $1,920.00
Lokelma
sodium zirconium cyclosilicate
Box · from 1 per pack
Brand from $450.00
Lumizyme
Alglucosidase Alfa
By Sanofi
Vial · from 50 per pack
Brand $986.00
Magnesium Sulphate
Magnesium Sulphate
Pack sizes and pricing not listed yet
Micro‑K
Potassium Chloride
By G.L. Pharma
Capsules · from 50 per pack
Brand $20.00
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