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Metabolic Disorders

50 medicines listed.

Metabolic Disorders

Aldurazyme

Laronidase

By Sanofi (via Genzyme/BioMarin)

BrandRx required

Vial · from 1 per pack

500U/5ml

Brand $1,115.00

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Metabolic Disorders

Amvuttra

Vutrisiran

By Alnylam Pharmaceuticals

BrandRx required

Pack · from 1 per pack

25mg/0.5ml

Brand $166,475.00

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Metabolic Disorders

Carbaglu

Carglumic Acid

Rx required

Pack sizes and pricing not listed yet

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Metabolic Disorders

Cerdelga

Eliglustat

By Genzyme

BrandRx required

Capsules · from 56 per pack

84mg

Brand $34,500.00

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Metabolic Disorders

Cerezyme

Imiglucerase

By Genzyme

BrandRx required

Pack · from 1 per pack

400IU

Brand $2,745.00

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Metabolic Disorders

Crysvita

Burosumab

By Piramal Healthcare

BrandRx required

Vial · from 1 per pack

10mg20mg30mg

Brand from $5,225.00

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Metabolic Disorders

Cystadane

Betaine Anhydrous

By AOP Orphan

BrandRx required

Pack · from 1 per pack

180g

Brand $900.00

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Metabolic Disorders

Cystagon

Cysteamine Bitartrate

By Mylan

BrandRx required

Capsules · from 100 per pack

150mg

Brand $450.00

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Metabolic Disorders

Dojolvi

Triheptanoin

By Ultragenyx

BrandRx required

Pack · from 1 per pack

29g

Brand $12,350.00

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Metabolic Disorders

Dostinex

Cabergoline

By Pfizer

BrandRx required

Tablets · from 2 per pack

0.5mg

Brand from $32.00

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Metabolic Disorders

Elaprase

Idursulfase

By Takeda

BrandRx required

Pack · from 6 per pack

2mg/1ml

Brand $4,920.00

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Metabolic Disorders

Elelyso

Taliglucerase Alfa

By Pfizer

BrandRx required

Pack · from 1 per pack

200 Units

Brand $1,675.00

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Metabolic Disorders

Fabrazyme

Agalsidase Beta

By Sanofi

BrandRx required

Vial · from 35 per pack

35mg

Brand $5,390.00

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Metabolic Disorders

Galafold

Migalastat Hydrochloride

By Amicus Therapeutics

BrandRx required

Tablets · from 14 per pack

123mg

Brand $34,065.00

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Metabolic Disorders

GIVLAARI

Givosiran Sodium

By UNKNOWN

BrandRx required

Vial · from 1 per pack

189mg/ml

Brand $84,035.00

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Metabolic Disorders

Isturisa

Osilodrostat

By Recordati

BrandRx required

Tablets · from 60 per pack

1mg5mg10mg

Brand from $2,925.00

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Metabolic Disorders

Kanuma

Sebelipase Alfa

By Alexion Pharmaceuticals

BrandRx required

Vial · from 1 per pack

2mg/ml

Brand $14,435.00

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Metabolic Disorders

Kayexalate Powder

Polystyrene Sulphonate

By Sanofi

BrandRx required

Bottle · from 1 per pack

powder

Brand $83.00

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Metabolic Disorders

KUVAN

Sapropterin Dihydrochloride

By BioMarin

BrandRx required

Tablets · from 30 per pack

100mg

Brand from $785.00

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Metabolic Disorders

Lamzede

Velmanase alfa

By Chiesi

BrandRx required

Vial · from 1 per pack

10mg

Brand $1,920.00

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Metabolic Disorders

Lokelma

sodium zirconium cyclosilicate

BrandRx required

Box · from 1 per pack

5g10g

Brand from $450.00

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Metabolic Disorders

Lumizyme

Alglucosidase Alfa

By Sanofi

BrandRx required

Vial · from 50 per pack

50mg

Brand $986.00

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Metabolic Disorders

Magnesium Sulphate

Magnesium Sulphate

Rx required

Pack sizes and pricing not listed yet

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Metabolic Disorders

Micro‑K

Potassium Chloride

By G.L. Pharma

BrandRx required

Capsules · from 50 per pack

600mg

Brand $20.00

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Showing 1–24 of 50